FDA lifts hold on one of two Phase 3 gene editing studies by Intellia / Endpoints

Lei Lei Wu / endpoints - The FDA has allowed Intellia Therapeutics to resume one of its two pivotal trials of a gene editing therapy for transthyretin amyloidosis, which is a disease caused by misfolded proteins. Intellia

#healthcare #pharmaceuticals #publichealth #biotech #drugdevelopment #fda

Gene-editing therapy proves effective for Leber's hereditary optic neuropathy

4 wks / medicalxpress

China startup AccurEdit raises $75M for gene editing therapies

5 wks / endpoints / Ryan Cross

FDA lifts hold on one of two Phase 3 gene editing studies by Intellia

6 wks / endpoints / Lei Lei Wu

FDA lifts hold on Intellia’s phase 3 trial for genetic nerve disease

6 wks / beckershospitalreview / Ella Jeffries

Saturday, January 31, 2026, 7:22 am / permalink 18610 / 4 stories in 5 wks

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