Gene therapy improves hearing in 90% of patients with inherited deafness in largest trial of its kind
livescience - A new gene therapy tested in China has improved the hearing of 38 people who were born deaf due to mutations in a gene called OTOF.
AI Summary: A gene therapy for inherited deafness delivered dramatic results, restoring hearing in roughly 90% of treated patients in the largest trial of its kind. Investigators report durable improvements over follow-up, signaling a potential one-time intervention for certain genetic deafness types and challenging the notion that auditory loss is always irreversible. Hope, meet hard data.
- FDA approves first-ever gene therapy for inherited hearing loss (6)
- Primate study finds human-like genetic cause of blindness (1)
- Trial shows durable hearing restored in most patients (3)
FDA approves first-ever gene therapy for inherited hearing loss
Primate study finds human-like genetic cause of blindness
Trial shows durable hearing restored in most patients
Related Stories
Single‑infusion gene editing dramatically lowers LDL cholesterol in early trial / 5 wks
Gene therapy pioneers win Breakthrough Prize for CRISPR sickle‑cell work / 2 months
Analysis finds anti-amyloid Alzheimer's drugs lack meaningful benefit / 2 months
The peptide problem: Hype outruns evidence, researchers caution / 2 months
Researchers create world's first synthetic cell that grows and divides / 4 days
Stem cells show potent promise as a diabetes treatment / 6 wks
Mid‑stage Parkinson trial failure halts drug development plans / 7 wks
StackHealth RSS
You can now follow topics by RSS - browse the complete list of topics, people, and organizations. Or, try Research Funding, Pancreatic Cancer, Price Transparency, Autism and look for the RSS link.
StackHealth Time Machine